Department of Colorectal Surgery, Sir Run Run Shaw Hospital, Zhejiang University School of Medicine, Hangzhou, China.

Presa et al. use a mouse model of multiple sulfatase deficiency (MSD) to assess efficacy of bone marrow transplantation to increase sulfatase activity. Sulfatase activity is partially restored in ...

Sep. 9, 2024 — Researchers tested a preclinical model for an experimental gene therapy designed to treat multiple sulfatase deficiency (MSD), a disorder that affects the brain, lungs ...

Its commercial products include Vimizim, an enzyme replacement therapy for the treatment of mucopolysaccharidosis (MPS) IV ...

aro = aromatase, DOC = deoxycorticosterone, HSD = hydrosteroid dehydrogenase, HSO = hydrosteroid oxidoreductase, HSS = hydrosteroid sulfatase, KSR = ketosteroid reductase, R = reductase ...

National Pension Service raised its holdings in shares of BioMarin Pharmaceutical Inc. (NASDAQ:BMRN – Free Report) by 4.2% ...

此次获奖的NWU-CHINA-A团队由西北大学生命科学学院师生组成，雷蕾、李想、范铭沁、王弘靖、杨宇帆、瞿铱彤等6人赴法国巴黎参加线下盛会。2017年起，西北大学iGEM ...

Nov. 4, 2024 — Stem cells grown in microgravity aboard the International Space Station (ISS) have unique qualities that could one day help accelerate new biotherapies and heal complex disease ...

JCR Pharmaceuticals Co., Ltd. (TSE 4552; "JCR") announced the initiation of the first patient dosing in Japan in the Phase I clinical trial of JR-441, an investigational enzyme replacement therapy for ...

DNLI reports a wider-than-expected loss in the third quarter of 2024. Nonetheless, the pipeline progress has been encouraging.