This should lead to increased levels of LCA at birth. LCA, cholic acid (CA) and chenodeoxycholic acid (CDCA) were quantitated in stored dried blood from six newborn infants with EHBA and fourteen ...

Vivet Therapeutics Presents Three Posters on Cerebrotendinous Xanthomatosis Program and Novel AAV Gene Delivery Platform at European Society of Gene and Cell Therapy Annual Congress 2024 Paris ...